PERSPECTIVE
Published on 12 Dec 2022
Addressing the implementation gap in advanced therapeutics for spinal muscular atrophy in the era of newborn screening programs
doi 10.3389/fneur.2022.1064194
- 2,344 views
- 1 citation
- Frontiers in Neurology
- Neuromuscular Disorders and Peripheral Neuropathies
- Research Topics
- Gene Therapy for Neuromuscular Diseases
Gene Therapy for Neuromuscular Diseases
8,072
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Articles
REVIEW
Published on 28 Mar 2022
Therapeutic Strategies for Dystrophin Replacement in Duchenne Muscular Dystrophy
doi 10.3389/fmed.2022.859930
- 12,000 views
- 29 citations
REVIEW
Published on 05 Jan 2022
Adeno-Associated Virus (AAV)-Mediated Gene Therapy for Duchenne Muscular Dystrophy: The Issue of Transgene Persistence
doi 10.3389/fneur.2021.814174
- 22,366 views
- 50 citations
ORIGINAL RESEARCH
Published on 22 Sep 2021
Gene Therapy Overexpressing Neuregulin 1 Type I in Combination With Neuregulin 1 Type III Promotes Functional Improvement in the SOD1G93A ALS Mice
doi 10.3389/fneur.2021.693309
- 3,056 views
- 7 citations
Published in
Frontiers in Neurology
- Neuromuscular Disorders and Peripheral Neuropathies
Impact
- 35kTopic views
- 26kArticle views
- 8,072Article downloads