REVIEW
Published on 16 Sep 2021
Clinical Trials for Gene Therapy in Lysosomal Diseases With CNS Involvement
doi 10.3389/fmolb.2021.624988
- 7,374 views
- 32 citations
- Frontiers in Molecular Biosciences
- Molecular Diagnostics and Therapeutics
- Research Topics
- Neurodegenerative Lysosomal Storage Diseases (LSDs): Between Biology and Innovative Therapeutic Approaches
Neurodegenerative Lysosomal Storage Diseases (LSDs): Between Biology and Innovative Therapeutic Approaches
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Articles
REVIEW
Published on 12 Nov 2020
CNS-Targeting Therapies for Lysosomal Storage Diseases: Current Advances and Challenges
doi 10.3389/fmolb.2020.559804
- 11,832 views
- 53 citations
MINI REVIEW
Published on 18 Sep 2020
Human iPSC-Based Models for the Development of Therapeutics Targeting Neurodegenerative Lysosomal Storage Diseases
doi 10.3389/fmolb.2020.00224
- 5,175 views
- 17 citations
PERSPECTIVE
Published on 26 Aug 2020
Lysosomal Diseases and Neuropsychiatry: Opportunities to Rebalance the Mind
doi 10.3389/fmolb.2020.00177
- 5,197 views
- 12 citations
PERSPECTIVE
Published on 21 Jul 2020
Glutamate Carrier Involvement in Mitochondrial Dysfunctioning in the Brain White Matter
doi 10.3389/fmolb.2020.00151
- 6,412 views
- 11 citations
ORIGINAL RESEARCH
Published on 21 Jul 2020
In vitro Validation of Chimeric β-Galactosylceramidase Enzymes With Improved Enzymatic Activity and Increased Secretion
doi 10.3389/fmolb.2020.00167
- 3,342 views
- 6 citations
REVIEW
Published on 06 May 2020
Modeling Lysosomal Storage Diseases in the Zebrafish
doi 10.3389/fmolb.2020.00082
- 7,406 views
- 20 citations
REVIEW
Published on 15 Apr 2020
Pre-clinical Mouse Models of Neurodegenerative Lysosomal Storage Diseases
doi 10.3389/fmolb.2020.00057
- 9,554 views
- 20 citations
