AUTHOR=Ain Noor Ul , Saith Armaan , Ruan Audrey , Yang Ruhua , Burton Aaron , Mistry Pramod K. 

TITLE=Eliglustat substrate reduction therapy in children with Gaucher disease type 1

JOURNAL=Frontiers in Pediatrics

VOLUME=Volume 13 - 2025

YEAR=2025

URL=https://www.frontiersin.org/journals/pediatrics/articles/10.3389/fped.2025.1543136

DOI=10.3389/fped.2025.1543136

ISSN=2296-2360