AUTHOR=Meyer Sascha , Yeh E. Ann , Brunner Jürgen , Semler Oliver , Gropman Andrea 

TITLE=Editorial: New Therapeutic Options for Rare Diseases

JOURNAL=Frontiers in Pediatrics

VOLUME=9

YEAR=2022

URL=https://www.frontiersin.org/journals/pediatrics/articles/10.3389/fped.2021.832395

DOI=10.3389/fped.2021.832395

ISSN=2296-2360