AUTHOR=Cabré-Romans Júlia-Jié , Cuella-Martin Raquel TITLE=CRISPR-dependent base editing as a therapeutic strategy for rare monogenic disorders JOURNAL=Frontiers in Genome Editing VOLUME=Volume 7 - 2025 YEAR=2025 URL=https://www.frontiersin.org/journals/genome-editing/articles/10.3389/fgeed.2025.1553590 DOI=10.3389/fgeed.2025.1553590 ISSN=2673-3439