AUTHOR=Ugoji Chinenye , Heidt Julien , Largent Joan , Bratton Emily , Hester Laura , Keshavarzi Sareh , Turner Stuart , Mack Christina 

TITLE=Important tool in our rare disease toolbox: hybrid retrospective-prospective natural history studies serve well as external comparators for rare disease studies

JOURNAL=Frontiers in Drug Safety and Regulation

VOLUME=4

YEAR=2024

URL=https://www.frontiersin.org/journals/drug-safety-and-regulation/articles/10.3389/fdsfr.2024.1418050

DOI=10.3389/fdsfr.2024.1418050

ISSN=2674-0869