AUTHOR=Anderson Joseph S. , Silverman Jill L. , Lodigiani Alyse L. , Barbaduomo Camilla M. , Beegle Julie R. 

TITLE=Transduction of hematopoietic stem and progenitor cells by an MECP2 lentiviral vector improves Rett syndrome phenotypes

JOURNAL=Frontiers in Drug Discovery

VOLUME=5

YEAR=2025

URL=https://www.frontiersin.org/journals/drug-discovery/articles/10.3389/fddsv.2025.1545391

DOI=10.3389/fddsv.2025.1545391

ISSN=2674-0338